[1,2,4]Triazolo[1,5- a]pyrimidine Phosphodiesterase 2A Inhibitors: Structure and Free-Energy Perturbation-Guided Exploration

J Med Chem. 2020 Nov 12;63(21):12887-12910. doi: 10.1021/acs.jmedchem.0c01272. Epub 2020 Oct 26.

Abstract

We describe the hit-to-lead exploration of a [1,2,4]triazolo[1,5-a]pyrimidine phosphodiesterase 2A (PDE2A) inhibitor arising from high-throughput screening. X-ray crystallography enabled structure-guided design, leading to the identification of preferred substructural components. Further rounds of optimization used relative binding free-energy calculations to prioritize different substituents from the large accessible chemical space. The free-energy perturbation (FEP) calculations were performed for 265 putative PDE2A inhibitors, and 100 compounds were synthesized representing a relatively large prospective application providing unexpectedly active molecules with IC50's from 2340 to 0.89 nM. Lead compound 46 originating from the FEP calculations showed PDE2A inhibition IC50 of 1.3 ± 0.39 nM, ∼100-fold selectivity versus other PDE enzymes, clean cytochrome P450 profile, in vivo target occupancy, and promise for further lead optimization.

MeSH terms

  • Animals
  • Binding Sites
  • Brain / metabolism
  • Crystallography, X-Ray
  • Cyclic Nucleotide Phosphodiesterases, Type 2 / antagonists & inhibitors*
  • Cyclic Nucleotide Phosphodiesterases, Type 2 / metabolism
  • Drug Design
  • Half-Life
  • Humans
  • Inhibitory Concentration 50
  • Isoenzymes / antagonists & inhibitors
  • Isoenzymes / metabolism
  • Male
  • Microsomes, Liver / metabolism
  • Molecular Docking Simulation
  • Phosphodiesterase Inhibitors / chemistry*
  • Phosphodiesterase Inhibitors / metabolism
  • Phosphodiesterase Inhibitors / pharmacokinetics
  • Pyrimidines / chemistry*
  • Pyrimidines / metabolism
  • Pyrimidines / pharmacokinetics
  • Rats
  • Rats, Wistar
  • Stereoisomerism
  • Structure-Activity Relationship
  • Thermodynamics
  • Triazoles / chemistry*
  • Triazoles / metabolism
  • Triazoles / pharmacokinetics

Substances

  • Isoenzymes
  • Phosphodiesterase Inhibitors
  • Pyrimidines
  • Triazoles
  • triazolo(1,5-a)pyrimidine
  • Cyclic Nucleotide Phosphodiesterases, Type 2