Concentration-QTc Modeling of Ozanimod's Major Active Metabolites in Adult Healthy Subjects

CPT Pharmacometrics Syst Pharmacol. 2021 Feb;10(2):119-126. doi: 10.1002/psp4.12580. Epub 2021 Jan 5.

Abstract

Ozanimod, approved by regulatory agencies in multiple countries for the treatment of adults with relapsing multiple sclerosis, is a sphingosine 1-phosphate (S1P) receptor modulator, which binds with high affinity selectively to S1P receptor subtypes 1 and 5. The relationships between plasma concentrations of ozanimod and its major active metabolites, CC112273 and CC1084037, and the QTc interval (C-QTc) from a phase I multiple-dose study in healthy subjects were analyzed using nonlinear mixed effects modeling. QTc was modeled linearly as the sum of a sex-related fixed effect, baseline, and concentration-related random effects that incorporated interindividual and residual variability. Common linear, power, and maximum effect (Emax ) functions were assessed for characterizing the relationship of QTc with concentrations. Model goodness-of-fit and performance were evaluated by standard diagnostic tools, including a visual predictive check. The placebo-corrected change from baseline in QTc (ΔΔQTc) was estimated based on the developed C-QTc model using a nonparametric bootstrapping approach. QTc was better derived using a study-specific population formula (QTcP). Among the investigated functions, an Emax function most adequately described the relationship of QTcP with concentrations. Separate models for individual analytes characterized the C-QTcP relationship better than combined analytes models. Attributing QT prolongation independently to CC1084037 or CC112273, the upper bound of the 95% confidence interval of the predicted ΔΔQTcP was ~ 4 msec at the plateau of the Emax curves. Therefore, ΔΔQTcP is predicted to remain below 10 msec at the supratherapeutic concentrations of the major active metabolites.

Publication types

  • Clinical Trial, Phase I
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Administration, Oral
  • Adult
  • Case-Control Studies
  • Double-Blind Method
  • Electrocardiography / drug effects
  • Female
  • Healthy Volunteers
  • Heart Rate / drug effects
  • Humans
  • Indans / administration & dosage
  • Indans / adverse effects
  • Indans / pharmacokinetics*
  • Long QT Syndrome
  • Male
  • Multiple Sclerosis, Relapsing-Remitting / drug therapy*
  • Oxadiazoles / administration & dosage
  • Oxadiazoles / adverse effects
  • Oxadiazoles / pharmacokinetics*
  • Placebos / administration & dosage
  • Predictive Value of Tests
  • Sphingosine 1 Phosphate Receptor Modulators / administration & dosage
  • Sphingosine 1 Phosphate Receptor Modulators / adverse effects
  • Sphingosine 1 Phosphate Receptor Modulators / pharmacokinetics*
  • Sphingosine-1-Phosphate Receptors / metabolism*

Substances

  • Indans
  • Oxadiazoles
  • Placebos
  • Sphingosine 1 Phosphate Receptor Modulators
  • Sphingosine-1-Phosphate Receptors
  • ozanimod