The anti-tumor effects of cetuximab in combination with VTX-2337 are T cell dependent

Sci Rep. 2021 Jan 15;11(1):1535. doi: 10.1038/s41598-020-80957-z.

Abstract

The Toll-like receptor 8 (TLR8) agonist VTX-2337 (motolimod) is an anti-cancer immunotherapeutic agent that is believed to augment natural killer (NK) and dendritic cell (DC) activity. The goal of this work is to examine the role of TLR8 expression/activity in head and neck squamous cell carcinoma (HNSCC) to facilitate the prediction of responders to VTX-2337-based therapy. The prognostic role of TLR8 expression in HNSCC patients was assessed by TCGA and tissue microarray analyses. The anti-tumor effect of VTX-2337 was determined in SCCVII/C3H, mEERL/C57Bl/6 and TUBO-human EGFR/BALB/c syngeneic mouse models. The effect of combined VTX-2337 and cetuximab treatment on tumor growth, survival and immune cell recruitment was assessed. TLR8 expression was associated with CD8+ T cell infiltration and favorable survival outcomes. VTX-2337 delayed tumor growth in all 3 syngeneic mouse models and significantly increased the survival of cetuximab-treated mice. The anti-tumor effects of VTX-2337+ cetuximab were accompanied by increased splenic lymphoid DCs and IFNγ+ CD4+ and tumor-specific CD8+ T cells. Depletion of CD4+ T cells, CD8+ T cells and NK cells were all able to abolish the anti-tumor effect of VTX-2337+ cetuximab. Altogether, VTX-2337 remains promising as an adjuvant for cetuximab-based therapy however patients with high TLR8 expression may be more likely to derive benefit from this drug combination compared to patients with low TLR8 expression.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Antibody-Dependent Cell Cytotoxicity / immunology
  • Antineoplastic Agents / pharmacology
  • Benzazepines / metabolism
  • Benzazepines / pharmacology*
  • Biomarkers, Pharmacological
  • CD8-Positive T-Lymphocytes / immunology
  • Cell Line, Tumor
  • Cetuximab / metabolism
  • Cetuximab / pharmacology*
  • Cytokines / metabolism
  • Databases, Genetic
  • Female
  • Gene Expression / genetics
  • Gene Expression Regulation, Neoplastic / genetics
  • Humans
  • Killer Cells, Natural / immunology
  • Male
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C3H
  • Mice, Inbred C57BL
  • Neoplasms / drug therapy
  • Neoplasms / immunology
  • Squamous Cell Carcinoma of Head and Neck / drug therapy
  • Squamous Cell Carcinoma of Head and Neck / immunology
  • T-Lymphocytes / immunology
  • T-Lymphocytes / metabolism*
  • Toll-Like Receptor 8 / drug effects
  • Toll-Like Receptor 8 / genetics
  • Toll-Like Receptor 8 / metabolism

Substances

  • Antineoplastic Agents
  • Benzazepines
  • Biomarkers, Pharmacological
  • Cytokines
  • TLR8 protein, human
  • Toll-Like Receptor 8
  • VTX-2337
  • Cetuximab