Treatment of infantile fibrosarcoma associated to an abdominal aortic aneurysm with larotrectinib: a case report

Pediatr Hematol Oncol. 2021 Aug;38(5):504-509. doi: 10.1080/08880018.2021.1889730. Epub 2021 Feb 24.

Abstract

Infantile fibrosarcoma (IFS) is a rare pediatric tumor which often presents the ETV6-NTRK3 gene fusion. NTRK3 encodes the neurotrophin-3 growth factor receptor tyrosine kinase, a druggable therapeutic target. Selective tropomyosin receptor kinase (TRK) inhibitors, such as larotrectinib, have shown efficacy and safety in the treatment of IFS. We report a case of an abdominal IFS diagnosed in a newborn associated with an aortic aneurysm that was successfully treated with larotrectinib without relevant adverse effects.

Keywords: Abdominal aneurysm; infantile fibrosarcoma; larotrectinib; tropomyosin receptor kinase inhibitor.

Publication types

  • Case Reports

MeSH terms

  • Abdominal Neoplasms / complications
  • Abdominal Neoplasms / diagnosis
  • Abdominal Neoplasms / drug therapy*
  • Aortic Aneurysm, Abdominal / complications*
  • Female
  • Fibrosarcoma / complications
  • Fibrosarcoma / diagnosis
  • Fibrosarcoma / drug therapy*
  • Humans
  • Infant
  • Infant, Newborn
  • Protein Kinase Inhibitors / therapeutic use*
  • Pyrazoles / therapeutic use*
  • Pyrimidines / therapeutic use*

Substances

  • Protein Kinase Inhibitors
  • Pyrazoles
  • Pyrimidines
  • larotrectinib