A hemizygous mutation in the FOXP3 gene (IPEX syndrome) resulting in recurrent X-linked fetal hydrops: a case report

BMC Med Genomics. 2021 Feb 26;14(1):58. doi: 10.1186/s12920-021-00901-6.

Abstract

Background: Fetal hydrops is excessive extravasation of fluid into the third space in a fetus, which could be due to a wide differential of underlying pathology. IPEX (immune dysregulation, polyendocrinopathy, enteropathy, X-linked) syndrome primarily affects males. It is a monogenic primary immunodeficiency syndrome of X-linked recessive inheritance due to FOXP3 gene variants. It is characterised by the development of multiple autoimmune disorders in affected individuals.

Case presentation: We present a rare cause of male fetal hydrops in the context of IPEX syndrome and discuss FOXP3 gene variants as a differential for 'unexplained' fetal hydrops that may present after the first trimester.

Discussion and conclusions: In all similar cases, the pathological process begins during intrauterine life. Furthermore, there are no survivors described. Consequently, this variant should be considered as a severe one, associated with intrauterine life onset and fatal course, i.e., the most severe IPEX phenotype.

Keywords: FOXP3; Fetal hydrops; IPEX syndrome; In utero transfusion.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Diabetes Mellitus, Type 1 / complications
  • Diabetes Mellitus, Type 1 / congenital
  • Diabetes Mellitus, Type 1 / genetics
  • Diarrhea / genetics
  • Female
  • Forkhead Transcription Factors* / genetics
  • Genetic Diseases, X-Linked* / genetics
  • Humans
  • Hydrops Fetalis* / genetics
  • Immune System Diseases / congenital
  • Immune System Diseases / genetics
  • Male
  • Mutation
  • Pregnancy

Substances

  • Forkhead Transcription Factors
  • FOXP3 protein, human

Supplementary concepts

  • Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome