Developmental basis of trachea-esophageal birth defects

Dev Biol. 2021 Sep:477:85-97. doi: 10.1016/j.ydbio.2021.05.015. Epub 2021 May 21.

Abstract

Trachea-esophageal defects (TEDs), including esophageal atresia (EA), tracheoesophageal fistula (TEF), and laryngeal-tracheoesophageal clefts (LTEC), are a spectrum of life-threatening congenital anomalies in which the trachea and esophagus do not form properly. Up until recently, the developmental basis of these conditions and how the trachea and esophagus arise from a common fetal foregut was poorly understood. However, with significant advances in human genetics, organoids, and animal models, and integrating single cell genomics with high resolution imaging, we are revealing the molecular and cellular mechanisms that orchestrate tracheoesophageal morphogenesis and how disruption in these processes leads to birth defects. Here we review the current understanding of the genetic and developmental basis of TEDs. We suggest future opportunities for integrating developmental mechanisms elucidated from animals and organoids with human genetics and clinical data to gain insight into the genotype-phenotype basis of these heterogeneous birth defects. Finally, we envision how this will enhance diagnosis, improve treatment, and perhaps one day, lead to new tissue replacement therapy.

Keywords: Congenital anomalies; Development; EA/TEF; Esophageal atresia; Esophagus; Foregut; Laryngotracheoesophageal cleft; Trachea; Tracheoesophageal fistula.

Publication types

  • Research Support, N.I.H., Extramural
  • Review

MeSH terms

  • Animals
  • Digestive System Abnormalities / diagnosis
  • Digestive System Abnormalities / etiology
  • Digestive System Abnormalities / genetics
  • Disease Models, Animal
  • Esophagus / abnormalities*
  • Esophagus / embryology
  • Humans
  • Organoids / embryology
  • Trachea / abnormalities*
  • Trachea / embryology