A Possible Sterilizing Cure of HIV-1 Infection Without Stem Cell Transplantation

Ann Intern Med. 2022 Jan;175(1):95-100. doi: 10.7326/L21-0297. Epub 2021 Nov 16.

Abstract

Background: A sterilizing cure of HIV-1 infection has been reported in 2 persons living with HIV-1 who underwent allogeneic hematopoietic stem cell transplantations from donors who were homozygous for the CCR5Δ32 gene polymorphism. However, this has been considered elusive during natural infection.

Objective: To evaluate persistent HIV-1 reservoir cells in an elite controller with undetectable HIV-1 viremia for more than 8 years in the absence of antiretroviral therapy.

Design: Detailed investigation of virologic and immunologic characteristics.

Setting: Tertiary care centers in Buenos Aires, Argentina, and Boston, Massachusetts.

Patient: A patient with HIV-1 infection and durable drug-free suppression of HIV-1 replication.

Measurements: Analysis of genome-intact and replication-competent HIV-1 using near-full-length individual proviral sequencing and viral outgrowth assays, respectively; analysis of HIV-1 plasma RNA by ultrasensitive HIV-1 viral load testing.

Results: No genome-intact HIV-1 proviruses were detected in analysis of a total of 1.188 billion peripheral blood mononuclear cells and 503 million mononuclear cells from placental tissues. Seven defective proviruses, some of them derived from clonally expanded cells, were detected. A viral outgrowth assay failed to retrieve replication-competent HIV-1 from 150 million resting CD4+ T cells. No HIV-1 RNA was detected in 4.5 mL of plasma.

Limitations: Absence of evidence for intact HIV-1 proviruses in large numbers of cells is not evidence of absence of intact HIV-1 proviruses. A sterilizing cure of HIV-1 can never be empirically proved.

Conclusion: Genome-intact and replication-competent HIV-1 were not detected in an elite controller despite analysis of massive numbers of cells from blood and tissues, suggesting that this patient may have naturally achieved a sterilizing cure of HIV-1 infection. These observations raise the possibility that a sterilizing cure may be an extremely rare but possible outcome of HIV-1 infection.

Primary funding source: National Institutes of Health and Bill & Melinda Gates Foundation.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Argentina
  • CD4-Positive T-Lymphocytes / immunology
  • Female
  • Genotype
  • HIV Infections / genetics*
  • HIV Infections / immunology*
  • HIV-1 / genetics*
  • High-Throughput Nucleotide Sequencing
  • Host-Pathogen Interactions
  • Humans
  • Massachusetts
  • Pregnancy
  • Pregnancy Outcome
  • Proviruses / genetics
  • Proviruses / immunology
  • Receptors, CCR5 / genetics*
  • Viral Load
  • Viremia / virology
  • Virus Replication / immunology

Substances

  • CCR5 protein, human
  • Receptors, CCR5