Ruxolitinib for the treatment of steroid refractory pediatric chronic graft-versus-host disease

Pediatr Dermatol. 2022 May;39(3):432-433. doi: 10.1111/pde.14965. Epub 2022 Mar 2.

Abstract

Chronic graft-versus-host disease (cGVHD) of the skin is a serious cause of long-term morbidity and mortality among patients who receive hematopoietic stem cell transplants. Systemic corticosteroids remain first-line treatment for cutaneous cGVHD; however, there is currently no consensus on second-line therapy for steroid-refractory disease. We herein present a case of a pediatric patient with severe cGVHD of the skin, nonresponsive to corticosteroids, who was successfully treated with a prolonged course of ruxolitinib with minimal side effects.

Keywords: chronic skin graft-versus-host disease; corticosteroid-refractory graft-versus-host disease; hematopoietic stem cell transplant; ruxolitinib.

Publication types

  • Case Reports

MeSH terms

  • Adrenal Cortex Hormones / therapeutic use
  • Child
  • Chronic Disease
  • Graft vs Host Disease* / drug therapy
  • Graft vs Host Disease* / etiology
  • Hematopoietic Stem Cell Transplantation* / adverse effects
  • Humans
  • Nitriles
  • Pyrazoles
  • Pyrimidines
  • Retrospective Studies
  • Steroids / therapeutic use

Substances

  • Adrenal Cortex Hormones
  • Nitriles
  • Pyrazoles
  • Pyrimidines
  • Steroids
  • ruxolitinib