Mycophenolate mofetil for immune checkpoint inhibitor-related hepatotoxicity relapsing during dose reduction of corticosteroid: A report of two cases and literature review

Cancer Rep (Hoboken). 2022 Sep;5(9):e1624. doi: 10.1002/cnr2.1624. Epub 2022 May 16.

Abstract

Background: Immune checkpoint inhibitors (ICIs) sometimes cause immune-related liver injury, which can lead to cessation of treatment, hospitalization, and even mortality. Although high-dose corticosteroids are usually effective in treatment of ICI-related liver injury, one fifth of affected patients require additional immunosuppressive therapy. It remains uncertain how best to treat ICI-related liver injury that relapses under corticosteroid therapy after temporary remission.

Case: Here we report two cases of ICI-related liver injury successfully treated with mycophenolate mofetil (MMF). In the first case, a 74-year-old man with stage IIIA lung cancer underwent curative chemoradiotherapy. After the second infusion of durvalumab, grade 3 ICI-related liver injury (mixed pattern) developed. In the second case, a 46-year-old man with stage IVB lung cancer received pembrolizumab-containing chemotherapy. After the first cycle, grade 2 ICI-related hepatitis developed. In the both cases, liver injury improved with high-dose prednisolone but relapsed during tapering of the drug. After liver biopsy was performed to confirm the diagnosis of ICI-related liver injury, MMF (2000 mg/day) was added. MMF was effective for both patients and permitted discontinuation or reduction of prednisolone.

Conclusion: MMF appears to be an appropriate treatment option for ICI-related liver injury that respond to high-dose corticosteroids but relapse during steroid tapering.

Keywords: durvalumab; immune checkpoint inhibitor; immune checkpoint inhibitor hepatotoxicity; immune checkpoint inhibitor-related adverse event; mycophenolate mofetil; pembrolizumab.

Publication types

  • Case Reports
  • Review

MeSH terms

  • Adrenal Cortex Hormones
  • Aged
  • Chemical and Drug Induced Liver Injury* / diagnosis
  • Chemical and Drug Induced Liver Injury* / drug therapy
  • Chemical and Drug Induced Liver Injury* / etiology
  • Drug Tapering
  • Humans
  • Immune Checkpoint Inhibitors / adverse effects
  • Lung Neoplasms* / chemically induced
  • Lung Neoplasms* / drug therapy
  • Male
  • Middle Aged
  • Mycophenolic Acid / adverse effects
  • Neoplasm Recurrence, Local / drug therapy
  • Prednisolone / adverse effects

Substances

  • Adrenal Cortex Hormones
  • Immune Checkpoint Inhibitors
  • Prednisolone
  • Mycophenolic Acid