Additional evidence for the role of chromosomal imbalances and SOX8, ZNRF3 and HHAT gene variants in early human testis development

Reprod Biol Endocrinol. 2023 Jan 11;21(1):2. doi: 10.1186/s12958-022-01045-7.

Abstract

Background: Forty-six ,XY Differences/Disorders of Sex Development (DSD) are characterized by a broad phenotypic spectrum ranging from typical female to male with undervirilized external genitalia, or more rarely testicular regression with a typical male phenotype. Despite progress in the genetic diagnosis of DSD, most 46,XY DSD cases remain idiopathic.

Methods: To determine the genetic causes of 46,XY DSD, we studied 165 patients of Tunisian ancestry, who presented a wide range of DSD phenotypes. Karyotyping, candidate gene sequencing, and whole-exome sequencing (WES) were performed.

Results: Cytogenetic abnormalities, including a high frequency of sex chromosomal anomalies (85.4%), explained the phenotype in 30.9% (51/165) of the cohort. Sanger sequencing of candidate genes identified a novel pathogenic variant in the SRY gene in a patient with 46,XY gonadal dysgenesis. An exome screen of a sub-group of 44 patients with 46,XY DSD revealed pathogenic or likely pathogenic variants in 38.6% (17/44) of patients.

Conclusion: Rare or novel pathogenic variants were identified in the AR, SRD5A2, ZNRF3, SOX8, SOX9 and HHAT genes. Overall our data indicate a genetic diagnosis rate of 41.2% (68/165) in the group of 46,XY DSD.

Keywords: 46,XY DSD; Cytogenetic abnormalities; Disorders of sex development (DSD); Whole exome sequencing(WES).

MeSH terms

  • 3-Oxo-5-alpha-Steroid 4-Dehydrogenase / genetics
  • Acyltransferases* / genetics
  • Female
  • Gonadal Dysgenesis, 46,XY* / genetics
  • Humans
  • Male
  • Membrane Proteins / genetics
  • Mutation
  • Phenotype
  • SOXE Transcription Factors* / genetics
  • Sex Differentiation
  • Sexual Development* / genetics
  • Testis* / growth & development
  • Ubiquitin-Protein Ligases* / genetics

Substances

  • 3-Oxo-5-alpha-Steroid 4-Dehydrogenase
  • Acyltransferases
  • HHAT protein, human
  • Membrane Proteins
  • SOX8 protein, human
  • SOXE Transcription Factors
  • SRD5A2 protein, human
  • Ubiquitin-Protein Ligases
  • ZNRF3 protein, human