Novel breakthrough in the treatment of sphingomyelinase deficiency

Int J Surg. 2023 Feb 1;109(2):141-142. doi: 10.1097/JS9.0000000000000102.
No abstract available

MeSH terms

  • Humans
  • Niemann-Pick Disease, Type A*
  • Sphingomyelin Phosphodiesterase / genetics

Substances

  • Sphingomyelin Phosphodiesterase