Glucocorticoid withdrawal and glucocorticoid-induced adrenal insufficiency: Study protocol of the randomized controlled «TOASST" (Taper Or Abrupt Steroid STop) multicenter trial

PLoS One. 2023 Apr 5;18(4):e0281585. doi: 10.1371/journal.pone.0281585. eCollection 2023.

Abstract

Background: Despite the widespread use of glucocorticoids in inflammatory and autoimmune disorders, there is uncertainty about the safe cessation of long-term systemic treatment, as data from prospective trials are largely missing. Due to potential disease relapse or glucocorticoid-induced hypocortisolism, the drug is often tapered to sub-physiological doses rather than stopped when the underlying disease is clinically stable, increasing the cumulative drug exposure. Conversely, the duration of exposure to glucocorticoids should be minimized to lower the risk of side effects.

Methods: We designed a multicenter, randomized, triple-blinded, placebo-controlled trial to test the clinical noninferiority of abrupt glucocorticoid stop compared to tapering after ≥28 treatment days with ≥420 mg cumulative and ≥7.5 mg mean daily prednisone-equivalent dose. 573 adult patients treated systemically for various disorders will be included after their underlying disease has been stabilized. Prednisone in tapering doses or matching placebo is administered over 4 weeks. A 250 mg ACTH-test, the result of which will be revealed a posteriori, is performed at study inclusion; all patients are instructed on glucocorticoid stress cover dosing. Follow-up is for 6 months. The composite primary outcome measure is time to hospitalization, death, initiation of unplanned systemic glucocorticoid therapy, or adrenal crisis. Secondary outcomes include the individual components of the primary outcome, cumulative glucocorticoid doses, signs and symptoms of hypocortisolism, and the performance of the ACTH test in predicting the clinical outcome. Cox proportional hazard, linear, and logistic regression models will be used for statistical analysis.

Conclusion: This trial aims to demonstrate the clinical noninferiority and safety of abrupt treatment cessation after ≥28 days of systemic glucocorticoid therapy in patients with stabilized underlying disease.

Trial registration: ClinicalTrials.gov Identifier: NCT03153527; EUDRA-CT: 2020-005601-48 https://clinicaltrials.gov/ct2/show/NCT03153527?term=NCT03153527&draw=2&rank=1.

Publication types

  • Clinical Trial Protocol
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adrenal Insufficiency* / chemically induced
  • Adrenocorticotropic Hormone
  • Adult
  • Glucocorticoids* / adverse effects
  • Glucocorticoids* / therapeutic use
  • Humans
  • Multicenter Studies as Topic
  • Neoplasm Recurrence, Local / drug therapy
  • Prednisone / adverse effects
  • Prednisone / therapeutic use
  • Prospective Studies
  • Randomized Controlled Trials as Topic
  • Withholding Treatment

Substances

  • Adrenocorticotropic Hormone
  • Glucocorticoids
  • Prednisone

Associated data

  • ClinicalTrials.gov/NCT03153527
  • EudraCT/2020-005601-48

Grants and funding

This trial is supported by the Swiss National Science Foundation (grant no. 32003B_163133; https://www.snf.ch/en), the Hemmi Foundation (Therwil, Switzerland; https://stiftungen.stiftungschweiz.ch/organisation/hemmi-stiftung), the Gebauer Foundation (Zürich, Switzerland; https://www.gebauerstiftung.ch), the Hugo und Elsa Isler-Fund (Aarau, Switzerland; https://ichgcp.net/de/clinical-trials-registry/research/list?spons=Hugo%20%26%20Elsa%20Isler%20Foundation), funds from the University of Basel, Faculty of Medicine (https://www.unibas.ch/en/Faculties-Departments.html?id=490672ae-4f1a-4ffd-964f-58b38dda5a95), the LOA Fund for Quality and Research (Solothurn, Switzerland; https://www.guidestar.org/profile/45-2534204). The LOA Fund is administered by a consortium of Swiss health insurance companies and is augmented through premium payments by citizens insured in Switzerland. The funders had and have no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript.