AT7867 promotes pancreatic progenitor differentiation of human iPSCs

Stem Cell Reports. 2023 Nov 14;18(11):2084-2095. doi: 10.1016/j.stemcr.2023.10.005. Epub 2023 Nov 2.

Abstract

Generation of pure pancreatic progenitor (PP) cells is critical for clinical translation of stem cell-derived islets. Herein, we performed PP differentiation with and without AKT/P70 inhibitor AT7867 and characterized the resulting cells at protein and transcript level in vitro and in vivo upon transplantation into diabetic mice. AT7867 treatment increased the percentage of PDX1+NKX6.1+ (-AT7867: 50.9% [IQR 48.9%-53.8%]; +AT7867: 90.8% [IQR 88.9%-93.7%]; p = 0.0021) and PDX1+GP2+ PP cells (-AT7867: 39.22% [IQR 36.7%-44.1%]; +AT7867: 90.0% [IQR 88.2%-93.6%]; p = 0.0021). Transcriptionally, AT7867 treatment significantly upregulated PDX1 (p = 0.0001), NKX6.1 (p = 0.0005), and GP2 (p = 0.002) expression compared with controls, while off-target markers PODXL (p < 0.0001) and TBX2 (p < 0.0001) were significantly downregulated. Transplantation of AT7867-treated PPs resulted in faster hyperglycemia reversal in diabetic mice compared with controls (time and group: p < 0.0001). Overall, our data show that AT7867 enhances PP cell differentiation leading to accelerated diabetes reversal.

Keywords: bioreactor; cell therapy; diabetes; human induced pluripotent stem cells; islet cell transplant; islet differentiation; pancreatic progenitors; scalability; vertical wheel bioreactor; β cells.

MeSH terms

  • Animals
  • Cell Differentiation
  • Diabetes Mellitus, Experimental* / metabolism
  • Homeodomain Proteins / genetics
  • Homeodomain Proteins / metabolism
  • Humans
  • Induced Pluripotent Stem Cells* / metabolism
  • Insulin-Secreting Cells* / metabolism
  • Mice
  • Pancreas

Substances

  • AT 7867
  • Homeodomain Proteins