SMARCA4-Deficient Undifferentiated Tumor of the Esophagus: Diagnostic Pitfalls in Immunohistochemical Profiles

Int J Surg Pathol. 2024 Oct;32(7):1292-1302. doi: 10.1177/10668969241228290. Epub 2024 Mar 18.

Abstract

SMARCA4-deficient undifferentiated tumors (SMARCA4-UT) are a newly described entity and are typically seen in the thoracic cavity. However, these tumors have been described in other body sites, including the esophagus. These tumors are rare, aggressive neoplasms, characterized by the loss of protein product of SMARCA4 (Brahma-related gene-1) and the preservation of INI1 (SMARCB1) expression. Here, we present two tumors of SMARCA4-UT of the esophagus with its microscopic appearance and immunohistochemical profile. We also include a literature review of SMARCA4-deficient tumors of the tubular gastrointestinal tract with their immunohistochemical and mismatch repair profiles for each specimen. Due to its non-specific histologic appearance and variable staining in expanded immunohistochemical panels, this tumor frequently overlaps with other tumor types, making the diagnosis of SMARCA4-UT challenging. These tumors are often associated with intestinal metaplasia of the esophagus and are thought to represent a high-grade undifferentiated transformation of a conventional esophageal adenocarcinoma. These tumors are typically associated with poor clinical outcomes and have poor response to conventional therapies. Currently, there are no standard guidelines for treatment of these tumors; however, palliative radiotherapy and systemic chemotherapy may provide benefit. More recently, immunotherapy and novel therapeutic targets have shown some promise for these patients.

Keywords: BRG1; SMARCA4; esophagus; immunohistochemistry; pitfalls; undifferentiated.

Publication types

  • Review

MeSH terms

  • Adenocarcinoma / diagnosis
  • Adenocarcinoma / pathology
  • Biomarkers, Tumor* / analysis
  • Biomarkers, Tumor* / metabolism
  • DNA Helicases* / deficiency
  • DNA Helicases* / genetics
  • DNA Helicases* / metabolism
  • Diagnosis, Differential
  • Esophageal Neoplasms* / diagnosis
  • Esophageal Neoplasms* / pathology
  • Esophagus / pathology
  • Humans
  • Immunohistochemistry*
  • Nuclear Proteins* / deficiency
  • Nuclear Proteins* / genetics
  • Nuclear Proteins* / metabolism
  • Transcription Factors* / deficiency
  • Transcription Factors* / genetics
  • Transcription Factors* / metabolism

Substances

  • Biomarkers, Tumor
  • DNA Helicases
  • Nuclear Proteins
  • SMARCA4 protein, human
  • Transcription Factors