Matching study design to prescribing intention: The prevalent new-user design for studying abuse-deterrent formulations of opioids

Pharmacoepidemiol Drug Saf. 2024 May;33(5):e5805. doi: 10.1002/pds.5805.

Abstract

Purpose: In drug studies, research designs requiring no prior exposure to certain drug classes may restrict important populations. Since abuse-deterrent formulations (ADF) of opioids are routinely prescribed after other opioids, choice of study design, identification of appropriate comparators, and addressing confounding by "indication" are important considerations in ADF post-marketing studies.

Methods: In a retrospective cohort study using claims data (2006-2018) from a North Carolina private insurer [NC claims] and Merative MarketScan [MarketScan], we identified patients (18-64 years old) initiating ADF or non-ADF extended-release/long-acting (ER/LA) opioids. We compared patient characteristics and described opioid treatment history between treatment groups, classifying patients as traditional (no opioid claims during prior six-month washout period) or prevalent new users.

Results: We identified 8415 (NC claims) and 147 978 (MarketScan) ADF, and 10 114 (NC claims) and 232 028 (MarketScan) non-ADF ER/LA opioid initiators. Most had prior opioid exposure (ranging 64%-74%), and key clinical differences included higher prevalence of recent acute or chronic pain and surgery among patients initiating ADFs compared to non-ADF ER/LA initiators. Concurrent immediate-release opioid prescriptions at initiation were more common in prevalent new users than traditional new users.

Conclusions: Careful consideration of the study design, comparator choice, and confounding by "indication" is crucial when examining ADF opioid use-related outcomes.

Keywords: opioid analgesics; opioid prescribing; opioid related disorder; postmarketing evaluation studies; study design.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Abuse-Deterrent Formulations*
  • Adolescent
  • Adult
  • Analgesics, Opioid* / administration & dosage
  • Cohort Studies
  • Delayed-Action Preparations
  • Drug Prescriptions / statistics & numerical data
  • Female
  • Humans
  • Male
  • Middle Aged
  • North Carolina / epidemiology
  • Opioid-Related Disorders* / epidemiology
  • Opioid-Related Disorders* / prevention & control
  • Practice Patterns, Physicians'* / standards
  • Practice Patterns, Physicians'* / statistics & numerical data
  • Research Design*
  • Retrospective Studies
  • Young Adult

Substances

  • Analgesics, Opioid
  • Abuse-Deterrent Formulations
  • Delayed-Action Preparations