Survival of propionic acidemia patients with liver transplant

Mol Genet Metab Rep. 2024 May 27:40:101093. doi: 10.1016/j.ymgmr.2024.101093. eCollection 2024 Sep.

Abstract

Propionic acidemia (PA) is a rare metabolic disorder affecting amino acid metabolism. Liver transplantation improves some outcomes, but the impact on long-term survival remains unclear. A systematic literature review and survival analysis, identifying 94 PA patients who underwent transplantation, revealed a survival probability of 62% at age 33; while median survival was estimated at 40 years. These findings highlight a substantial survival deficit of PA patients compared to the general population despite liver transplantation.

Keywords: Life expectancy; Liver transplantation; Modeling; Propionic acidemia; Survival; Systematic literature review.