Studying the Effect of the Host Genetic Background of Juvenile Polyposis Development Using Collaborative Cross and Smad4 Knock-Out Mouse Models

Int J Mol Sci. 2024 May 27;25(11):5812. doi: 10.3390/ijms25115812.

Abstract

Juvenile polyposis syndrome (JPS) is a rare autosomal dominant disorder characterized by multiple juvenile polyps in the gastrointestinal tract, often associated with mutations in genes such as Smad4 and BMPR1A. This study explores the impact of Smad4 knock-out on the development of intestinal polyps using collaborative cross (CC) mice, a genetically diverse model. Our results reveal a significant increase in intestinal polyps in Smad4 knock-out mice across the entire population, emphasizing the broad influence of Smad4 on polyposis. Sex-specific analyses demonstrate higher polyp counts in knock-out males and females compared to their WT counterparts, with distinct correlation patterns. Line-specific effects highlight the nuanced response to Smad4 knock-out, underscoring the importance of genetic variability. Multimorbidity heat maps offer insights into complex relationships between polyp counts, locations, and sizes. Heritability analysis reveals a significant genetic basis for polyp counts and sizes, while machine learning models, including k-nearest neighbors and linear regression, identify key predictors, enhancing our understanding of juvenile polyposis genetics. Overall, this study provides new information on understanding the intricate genetic interplay in the context of Smad4 knock-out, offering valuable insights that could inform the identification of potential therapeutic targets for juvenile polyposis and related diseases.

Keywords: Smad4; collaborative cross mice; intestinal cancer; intestinal polyps; juvenile polyposis syndrome.

MeSH terms

  • Animals
  • Collaborative Cross Mice / genetics
  • Disease Models, Animal*
  • Female
  • Genetic Background
  • Intestinal Polyposis* / congenital
  • Intestinal Polyposis* / genetics
  • Intestinal Polyposis* / pathology
  • Intestinal Polyps / genetics
  • Intestinal Polyps / pathology
  • Male
  • Mice
  • Mice, Knockout
  • Neoplastic Syndromes, Hereditary* / genetics
  • Smad4 Protein* / genetics

Substances

  • Smad4 Protein
  • Smad4 protein, mouse

Supplementary concepts

  • Juvenile polyposis syndrome

Grants and funding

This study was supported by a core fund from Tel Aviv University and the Department of Oral and Maxillofacial Surgery, Baruch Padeh Medical Center, Poriya, Israel and the Ministry of the Negev, Galilee, and National Resilience.