Clinical utility of investigations in triple-negative thrombocytosis: A real-world, multicentre evaluation of UK practice

Br J Haematol. 2024 Oct;205(4):1411-1416. doi: 10.1111/bjh.19643. Epub 2024 Jul 14.

Abstract

Diagnosis of essential thrombocythaemia (ET) is challenging in patients lacking JAK2/CALR/MPL mutations. In a retrospective evaluation of 320 patients with 'triple-negative thrombocytosis', we assessed utility of bone marrow histology (90.9% of patients) and myeloid gene panel (MGP, 55.6%). Supportive histology ('myeloproliferative neoplasm-definite/probable', 36.8%) was associated with higher platelet counts and varied between centres. 14.6% MGP revealed significant variants: 3.4% JAK2/CALR/MPL and 11.2% other myeloid genes. Final clinical diagnosis was strongly predicted by histology, not MGP. 23.7% received cytoreduction (17.6% under 60 years). Real-world 'triple-negative' ET diagnosis currently depends heavily on histology; we advocate caution in MGP-negative cases and that specific guidelines are needed.

Keywords: diagnosis; molecular; myeloproliferative; thrombocytosis; triple‐negative.

Publication types

  • Multicenter Study

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Calreticulin / genetics
  • Female
  • Humans
  • Janus Kinase 2* / genetics
  • Male
  • Middle Aged
  • Mutation
  • Receptors, Thrombopoietin* / genetics
  • Retrospective Studies
  • Thrombocythemia, Essential / diagnosis
  • Thrombocythemia, Essential / genetics
  • Thrombocytosis / diagnosis
  • Thrombocytosis / genetics
  • United Kingdom

Substances

  • Janus Kinase 2
  • Receptors, Thrombopoietin
  • JAK2 protein, human
  • MPL protein, human
  • CALR protein, human
  • Calreticulin