Development of an engineered extracellular vesicles-based vaccine platform for combined delivery of mRNA and protein to induce functional immunity

J Control Release. 2024 Oct:374:550-562. doi: 10.1016/j.jconrel.2024.08.017. Epub 2024 Aug 30.

Abstract

mRNA incorporated in lipid nanoparticles (LNPs) became a new class of vaccine modality for induction of immunity against COVID-19 and ushered in a new era in vaccine development. Here, we report a novel, easy-to-execute, and cost effective engineered extracellular vesicles (EVs)-based combined mRNA and protein vaccine platform (EVX-M+P vaccine) and explore its utility in proof-of-concept immunity studies in the settings of cancer and infectious disease. As a first example, we engineered EVs, natural nanoparticle carriers shed by all cells, to contain ovalbumin mRNA and protein (EVOvaM+P vaccine) to serve as cancer vaccine against ovalbumin-expressing melanoma tumors. EVOvaM+P administration to mice with established melanoma tumors resulted in tumor regression associated with effective humoral and adaptive immune responses. As a second example, we generated engineered EVs that contain Spike (S) mRNA and protein to serve as a combined mRNA and protein vaccine (EVSpikeM+P vaccine) against SARS-CoV-2 infection. EVSpikeM+P vaccine administration in mice and baboons elicited robust production of neutralizing IgG antibodies against RBD (receptor binding domain) of S protein and S protein specific T cell responses. Our proof-of-concept study describes a new platform with an ability for rapid development of combination mRNA and protein vaccines employing EVs for deployment against cancer and other diseases.

MeSH terms

  • Animals
  • COVID-19 Vaccines* / administration & dosage
  • COVID-19 Vaccines* / immunology
  • COVID-19* / immunology
  • COVID-19* / prevention & control
  • Cancer Vaccines* / administration & dosage
  • Cancer Vaccines* / immunology
  • Cell Line, Tumor
  • Extracellular Vesicles* / immunology
  • Female
  • Humans
  • Lipids / administration & dosage
  • Lipids / chemistry
  • Liposomes
  • Melanoma / immunology
  • Melanoma / therapy
  • Mice
  • Mice, Inbred C57BL*
  • Nanoparticles* / administration & dosage
  • Nanoparticles* / chemistry
  • Ovalbumin* / administration & dosage
  • Ovalbumin* / immunology
  • RNA, Messenger* / administration & dosage
  • SARS-CoV-2 / immunology
  • Spike Glycoprotein, Coronavirus / genetics
  • Spike Glycoprotein, Coronavirus / immunology

Substances

  • COVID-19 Vaccines
  • Cancer Vaccines
  • RNA, Messenger
  • Ovalbumin
  • Spike Glycoprotein, Coronavirus
  • Lipid Nanoparticles
  • spike protein, SARS-CoV-2
  • Lipids
  • Liposomes