Targeted protein degradation using chimeric human E2 ubiquitin-conjugating enzymes

Commun Biol. 2024 Sep 19;7(1):1179. doi: 10.1038/s42003-024-06803-4.

Abstract

Proteins can be targeted for degradation by engineering biomolecules that direct them to the eukaryotic ubiquitination machinery. For instance, the fusion of an E3 ubiquitin ligase to a suitable target binding domain creates a 'biological Proteolysis-Targeting Chimera' (bioPROTAC). Here we employ an analogous approach where the target protein is recruited directly to a human E2 ubiquitin-conjugating enzyme via an attached target binding domain. Through rational design and screening we develop E2 bioPROTACs that induce the degradation of the human intracellular proteins SHP2 and KRAS. Using global proteomics, we characterise the target-specific and wider effects of E2 vs. VHL-based fusions. Taking SHP2 as a model target, we also employ a route to bioPROTAC discovery based on protein display libraries, yielding a degrader with comparatively weak affinity capable of suppressing SHP2-mediated signalling.

MeSH terms

  • HEK293 Cells
  • Humans
  • Protein Binding
  • Protein Tyrosine Phosphatase, Non-Receptor Type 11* / genetics
  • Protein Tyrosine Phosphatase, Non-Receptor Type 11* / metabolism
  • Proteolysis*
  • Proteomics / methods
  • Proto-Oncogene Proteins p21(ras) / genetics
  • Proto-Oncogene Proteins p21(ras) / metabolism
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / metabolism
  • Ubiquitin-Conjugating Enzymes* / genetics
  • Ubiquitin-Conjugating Enzymes* / metabolism
  • Ubiquitination

Substances

  • Ubiquitin-Conjugating Enzymes
  • Protein Tyrosine Phosphatase, Non-Receptor Type 11
  • Proto-Oncogene Proteins p21(ras)
  • KRAS protein, human
  • PTPN11 protein, human
  • Recombinant Fusion Proteins