Synthetic mismatches enable specific CRISPR-Cas12a-based detection of genome-wide SNVs tracked by ARTEMIS

Cell Rep Methods. 2024 Dec 16;4(12):100912. doi: 10.1016/j.crmeth.2024.100912. Epub 2024 Dec 6.

Abstract

Detection of pathogenic DNA variants is vital in cancer diagnostics and treatment monitoring. While CRISPR-based diagnostics (CRISPRdx) offer promising avenues for cost-effective, rapid, and point-of-care testing, achieving single-nucleotide detection fidelity remains challenging. We present an in silico pipeline that scans the human genome for targeting pathogenic mutations in the seed region (ARTEMIS), the most stringent crRNA domain. ARTEMIS identified 12% of pathogenic SNVs as Cas12a recognizable, including 928 cancer-associated variants such as BRAFV600E, BRCA2E1953∗, TP53V272M, and ALDH2E504K. Cas12a exhibited remarkable tolerance to single mismatches within the seed region. Introducing deliberate synthetic mismatches within the seed region yielded on-target activity with single-nucleotide fidelity. Both positioning and nucleobase types of mismatches influenced detection accuracy. With improved specificity, Cas12a could accurately detect and semi-quantify BRAFV600E in cfDNA from cell lines and patient liquid biopsies. These results provide insights toward rationalized crRNA design for high-fidelity CRISPRdx, supporting personalized and cost-efficient healthcare solutions in oncologic diagnostics.

Keywords: BRAF V600E; CP: Cancer biology; CP: Genetics; CRISPR; Cas12a; SNP; SNV; cancer; cfDNA; diagnostics; liquid biopsy; melanoma.

MeSH terms

  • Aldehyde Dehydrogenase, Mitochondrial / genetics
  • BRCA2 Protein / genetics
  • Bacterial Proteins
  • Base Pair Mismatch
  • CRISPR-Associated Proteins / genetics
  • CRISPR-Associated Proteins / metabolism
  • CRISPR-Cas Systems* / genetics
  • Endodeoxyribonucleases / genetics
  • Endodeoxyribonucleases / metabolism
  • Genome, Human / genetics
  • Humans
  • Neoplasms / diagnosis
  • Neoplasms / genetics
  • Polymorphism, Single Nucleotide / genetics
  • Proto-Oncogene Proteins B-raf / genetics
  • Tumor Suppressor Protein p53 / genetics

Substances

  • BRAF protein, human
  • Proto-Oncogene Proteins B-raf
  • ALDH2 protein, human
  • Cas12a protein
  • Aldehyde Dehydrogenase, Mitochondrial
  • Endodeoxyribonucleases
  • CRISPR-Associated Proteins
  • BRCA2 Protein
  • BRCA2 protein, human
  • Tumor Suppressor Protein p53
  • Bacterial Proteins