T helper 2 cell-directed immunotherapy eliminates precancerous skin lesions

J Clin Invest. 2025 Jan 2;135(1):e183274. doi: 10.1172/JCI183274.

Abstract

The continuous rise in skin cancer incidence highlights an imperative for improved skin cancer prevention. Topical calcipotriol-plus-5-fluorouracil (calcipotriol-plus-5-FU) immunotherapy effectively eliminates precancerous skin lesions and prevents squamous cell carcinoma (SCC) in patients. However, its mechanism of action remains unclear. Herein, we demonstrate that calcipotriol-plus-5-FU immunotherapy induces T helper type 2 (Th2) immunity, eliminating premalignant keratinocytes in humans. CD4+ Th2 cells were required and were sufficient downstream of thymic stromal lymphopoietin cytokine induction by calcipotriol to suppress skin cancer development. Th2-associated cytokines induced IL-24 expression in cancer cells, resulting in toxic autophagy and anoikis followed by apoptosis. Calcipotriol-plus-5-FU immunotherapy was dependent on IL-24 to suppress skin carcinogenesis in vivo. Collectively, our findings establish a critical role for Th2 immunity in cancer immunoprevention and highlight the Th2/IL-24 axis as an innovative target for skin cancer prevention and therapy.

Keywords: Dermatology; Immunotherapy; Oncology; Skin cancer; T cells.

MeSH terms

  • Animals
  • Calcitriol* / administration & dosage
  • Calcitriol* / analogs & derivatives
  • Calcitriol* / pharmacology
  • Carcinoma, Squamous Cell / immunology
  • Carcinoma, Squamous Cell / pathology
  • Carcinoma, Squamous Cell / therapy
  • Cytokines / immunology
  • Cytokines / metabolism
  • Fluorouracil* / administration & dosage
  • Fluorouracil* / therapeutic use
  • Humans
  • Immunotherapy
  • Interleukins* / genetics
  • Interleukins* / immunology
  • Keratinocytes / immunology
  • Keratinocytes / pathology
  • Mice
  • Precancerous Conditions* / immunology
  • Precancerous Conditions* / pathology
  • Precancerous Conditions* / prevention & control
  • Precancerous Conditions* / therapy
  • Skin Neoplasms* / immunology
  • Skin Neoplasms* / pathology
  • Skin Neoplasms* / therapy
  • Th2 Cells* / immunology

Substances

  • calcipotriene
  • Calcitriol
  • Interleukins
  • interleukin-24
  • Fluorouracil
  • Cytokines