Platelet-Targeted Gene Therapy for Hemophilia A with Inhibitor History
N Engl J Med
.
2025 Jan 23;392(4):412-414.
doi: 10.1056/NEJMc2415164.
Authors
Mary Eapen
1
,
Lynn M Malec
1
,
Myriam A Armant
2
,
Bryon D Johnson
3
,
Qizhen Shi
4
,
Huiqing Xu
3
,
Lily M Du
3
,
James H Jerkins
3
,
Lisa J Duffy
5
,
Frederic D Bushman
6
,
Carole Lee
6
,
Angelina Petrichenko
6
,
Peiman Hematti
3
,
Ruta Brazauskas
3
,
Shawn M Jobe
7
,
Parameswaran N Hari
3
,
David A Wilcox
3
Affiliations
1
Medical College of Wisconsin, Milwaukee, WI
[email protected]
.
2
Boston Children's Hospital, Boston, MA.
3
Medical College of Wisconsin, Milwaukee, WI.
4
Versiti Blood Research Institute, Milwaukee, WI.
5
Indiana University, Indianapolis, IN.
6
University of Pennsylvania, Philadelphia, PA.
7
Michigan State University, East Lansing, MI.
PMID:
39842018
DOI:
10.1056/NEJMc2415164
No abstract available
Publication types
Letter
Grants and funding
UO1TR0018414/TR/NCATS NIH HHS/United States
75N92019D00018-0-759201900074-1/HL/NHLBI NIH HHS/United States
RO1HL142791/HL/NHLBI NIH HHS/United States