Carrier detection in Sandhoff disease

Am J Hum Genet. 1978 Jan;30(1):38-45.

Abstract

Three new cases of Sandhoff disease are reported. One infant was the second affected child in a large family. The parents, who were cousins, were part of a large kindred from an isolated community in northern Saskatchewan. We assayed total and heat-stable hexosaminidases in 38 other members of the kindred and found two distinct cohorts. Sixteen individuals had low total and low heat-stable hexosaminidase and were diagnosed as carriers of Sandhoff disease. The values for the remainder were within normal limits. In a retrospective study of data from more than 14,000 Ashkenazi Jews, who were screened for Tay-Sachs disease, six were identified as Sandhoff carriers. Our data indicate that carrier detection requires measurement of both total and heat-stable enzyme activity.

Publication types

  • Case Reports
  • Comparative Study

MeSH terms

  • Consanguinity
  • Female
  • Gangliosidoses / diagnosis
  • Gangliosidoses / enzymology
  • Gangliosidoses / genetics*
  • Heterozygote
  • Hexosaminidases / blood*
  • Hot Temperature
  • Humans
  • Infant
  • Lipidoses / genetics
  • Male
  • Pedigree

Substances

  • Hexosaminidases