No abstract available
MeSH terms
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Adenosine Deaminase / deficiency
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Adrenoleukodystrophy / therapy*
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Bone Marrow Transplantation*
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Central Nervous System Diseases / therapy*
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Child
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Gaucher Disease / therapy*
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Humans
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Leukodystrophy, Metachromatic / therapy*
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Metabolic Diseases / classification
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Metabolic Diseases / therapy*
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Mucopolysaccharidoses / classification
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Mucopolysaccharidoses / therapy*
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Osteopetrosis / therapy
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Severe Combined Immunodeficiency / therapy