Severe combined immunodeficiency with absence of peripheral blood CD8+ T cells due to ZAP-70 deficiency

Cell Immunol. 1995 Oct 1;165(1):110-7. doi: 10.1006/cimm.1995.1193.

Abstract

During ontogeny, T lymphocytes are selected for CD4 or CD8 expression in part by their ability to signal properly through the TCR. Transmission of such signals requires the activation of specific cytoplasmic protein tyrosine kinases (PTKs) which lead to T-cell activation through poorly understood mechanisms. Recently, mutations in one such PTK, called ZAP-70, have been shown to be responsible for a rare, autosomal recessive form of severe combined immunodeficiency (SCID) in humans. This distinctive SCID syndrome is characterized by the selective absence of peripheral CD8+ T cells and by abundant circulating CD4+ T cells that fail to respond to TCR-mediated stimuli in vitro. In this report, we describe in detail the clinical and laboratory findings in one patient with ZAP-70 deficiency and discuss the insights provided by this disorder into the pathways of TCR signal transduction and T-cell development.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • B-Lymphocytes / immunology
  • CD4-Positive T-Lymphocytes / immunology
  • CD8-Positive T-Lymphocytes / immunology*
  • Female
  • Humans
  • Immunophenotyping / methods
  • Infant
  • Interleukin-2 / metabolism
  • Lymphocyte Activation / immunology
  • Lymphocyte Specific Protein Tyrosine Kinase p56(lck)
  • Lymphocytes / metabolism
  • Protein-Tyrosine Kinases / blood
  • Protein-Tyrosine Kinases / deficiency*
  • Proto-Oncogene Proteins / blood
  • Proto-Oncogene Proteins c-fyn
  • Receptors, Antigen, T-Cell / deficiency
  • Severe Combined Immunodeficiency / blood*
  • ZAP-70 Protein-Tyrosine Kinase

Substances

  • Interleukin-2
  • Proto-Oncogene Proteins
  • Receptors, Antigen, T-Cell
  • Protein-Tyrosine Kinases
  • FYN protein, human
  • Lymphocyte Specific Protein Tyrosine Kinase p56(lck)
  • Proto-Oncogene Proteins c-fyn
  • ZAP-70 Protein-Tyrosine Kinase
  • ZAP70 protein, human