Gene therapy for muscle diseases

Curr Opin Neurol. 1994 Oct;7(5):463-70. doi: 10.1097/00019052-199410000-00015.

Abstract

Duchenne muscular dystrophy involves progressive degeneration of the skeletal and cardiac muscles, resulting in premature death. A number of methods are currently being developed for the treatment of Duchenne muscular dystrophy and other neuromuscular disorders. A number of the viral vector systems, myoblast transfer, and direct injection techniques that are currently under investigation for the treatment of neuromuscular disorders are reviewed here.

Publication types

  • Review

MeSH terms

  • Dystrophin / genetics
  • Forecasting
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Humans
  • Muscular Dystrophies / classification
  • Muscular Dystrophies / genetics
  • Muscular Dystrophies / therapy
  • Neuromuscular Diseases / classification
  • Neuromuscular Diseases / genetics*
  • Neuromuscular Diseases / therapy
  • Transfection / genetics

Substances

  • Dystrophin