Spondyloepiphyseal dysplasia and precocious osteoarthritis in a family with an Arg75-->Cys mutation in the procollagen type II gene (COL2A1)

Hum Genet. 1993 Nov;92(5):499-505. doi: 10.1007/BF00216458.

Abstract

Direct sequencing of polymerase chain reaction (PCR)-amplified genomic DNA from a patient with spondyloepiphyseal dysplasia and precocious osteoarthritis revealed a single-base change in exon 11 of the type II procollagen gene (COL2A1), which produces an Arg-->Cys mutation in one allele. The proband is a member of a large Chilean kindred presenting with chondrodysplasia of the hips, knees, shoulders, elbows, and spine associated with severe, early-onset osteoarthritis. All affected individuals exhibit mildly short stature; in addition, five out of seven affected family members display shortened metacarpals or metatarsals. DNA from affected and unaffected family members was PCR-amplified and analysis of restriction digests of the products determined that the mutation segregated with the disease with a lod score of 2.2 at zero recombination. The mutation, which resides in the triple-helical region of type II procollagen at amino acid position 75, is the second example of an Arg-->Cys mutation in the COL2A1 gene in heritable cartilaginous disease and is the first example of a point mutation in the amino terminal region of the alpha 1(II) chain, that results in a spondyloepiphyseal dysplastic phenotype.

Publication types

  • Case Reports
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adolescent
  • Adult
  • Age of Onset
  • Aged
  • Amino Acid Sequence
  • Arginine / genetics
  • Base Sequence
  • Child
  • Cysteine / genetics
  • DNA Mutational Analysis
  • DNA Primers / genetics
  • Female
  • Genetic Linkage
  • Humans
  • Male
  • Middle Aged
  • Molecular Sequence Data
  • Osteoarthritis / complications
  • Osteoarthritis / genetics*
  • Osteochondrodysplasias / complications
  • Osteochondrodysplasias / genetics*
  • Pedigree
  • Point Mutation*
  • Polymerase Chain Reaction
  • Procollagen / genetics*

Substances

  • DNA Primers
  • Procollagen
  • Arginine
  • Cysteine