Characterization of a single base-pair deletion in neurofibromatosis type 1

Hum Mol Genet. 1993 Oct;2(10):1709-11. doi: 10.1093/hmg/2.10.1709.

Abstract

The gene which is responsible for neurofibromatosis type 1 (NF1) is located on chromosome 17 (17q11.2). The NF1 gene is approximately 350 kilobases (kb) long and exhibits an extremely high mutation rate; therefore, most patients are expected to have unique mutations. To date, relatively few mutations have been well characterized. We report here a de novo single base pair (bp) deletion in one NF1 allele in a patient diagnosed with NF1 and leukemia. We further characterized this mutation at the RNA level by allele-specific oligonucleotide (ASO) hybridization which demonstrated that the mutant allele is transcribed.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adolescent
  • Base Sequence
  • Chromosomes, Human, Pair 17*
  • DNA Mutational Analysis
  • Exons
  • Female
  • Genes, Neurofibromatosis 1*
  • Humans
  • Neurofibromatosis 1 / genetics*
  • Sequence Deletion*