A fragile X male with a broad smear on Southern blot analysis representing 100-500 CGG repeats and no methylation at the EagI site of the FMR-1 gene

Am J Med Genet. 1996 Aug 9;64(2):278-82. doi: 10.1002/(SICI)1096-8628(19960809)64:2<278::AID-AJMG9>3.0.CO;2-Q.

Abstract

Fragile X DNA studies were carried out on all obligate carriers of a large fragile X family with 10 mentally retarded individuals. One 64-year-old carrier man with an altered FMR-1 allele was not described as being mentally retarded or as having any limitations in function. He was married, raised 8 children, and worked as an auto mechanic. On examination, he had macrocephaly and mild macroorchidism but few of the other typical physical findings of males with fragile X syndrome. His Full Scale IQ is 73, and his Vineland Adaptive Behavior Composite is 73. On the Woodcock-Johnson Psycho-Educational Battery-Revised, he achieved standard scores of 64 in Reading, 55 in Math, and 83 in Knowledge. His DNA findings showed a broad smear on Southern blot analysis of 100-500 CGG repeats and no methylation at the EagI site upstream of the FMR-1 protein coding region. His FMR-1 protein production is 12% of normal. His daughters all have large premutations, with somatic instability in the size of the CGG repeat lengths. They all have evidence of academic underachievement and 2 have physical characteristics frequently described in individuals with fragile X.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Blotting, Southern
  • DNA / blood
  • DNA Methylation*
  • Deoxyribonucleases, Type II Site-Specific
  • Female
  • Fragile X Syndrome / genetics*
  • Fragile X Syndrome / physiopathology
  • Fragile X Syndrome / psychology
  • Genetic Carrier Screening*
  • Humans
  • Intellectual Disability / genetics
  • Male
  • Middle Aged
  • Pedigree
  • Restriction Mapping
  • Trinucleotide Repeats*

Substances

  • DNA
  • endodeoxyribonuclease XmaIII
  • Deoxyribonucleases, Type II Site-Specific