Nuclease sensitivity of permeabilized cells confirms altered chromatin formation at the fragile X locus

Somat Cell Mol Genet. 1996 Nov;22(6):435-41. doi: 10.1007/BF02369435.

Abstract

Fragile X syndrome is caused by the expansion and concomitant methylation of a CGG repeat in the 5' untranslated region of the FMR1 gene which results in the transcriptional silencing of the FMR1 gene, delayed replication of the FMR1 locus, and the formation of a folate sensitive fragile site (FRAXA) at Xq27.3. The mechanism by which repeat expansion and methylation causes these changes is unknown. An in vivo system in which cells were permeabilized with lysophosphatidylcholine followed by digestion with MspI endonuclease was utilized to assess the chromatin conformation at the fragile X locus. The FMR1 gene was inaccessible to MspI digestion in fragile X patients, but not in normal or carrier individuals, confirming that altered chromatin conformation results from the repeat expansion and methylation seen in fragile X syndrome.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Cell Line
  • Cell Membrane Permeability
  • Chromatin / enzymology
  • Chromatin / genetics*
  • Deoxyribonuclease HpaII / analysis*
  • Deoxyribonuclease HpaII / metabolism
  • Female
  • Fragile X Mental Retardation Protein
  • Fragile X Syndrome / enzymology
  • Fragile X Syndrome / genetics*
  • Humans
  • Male
  • Nerve Tissue Proteins / genetics*
  • RNA-Binding Proteins*
  • Repetitive Sequences, Nucleic Acid
  • X Chromosome*

Substances

  • Chromatin
  • FMR1 protein, human
  • Nerve Tissue Proteins
  • RNA-Binding Proteins
  • Fragile X Mental Retardation Protein
  • Deoxyribonuclease HpaII