HSV-TK gene transfer into donor lymphocytes for control of allogeneic graft-versus-leukemia

Science. 1997 Jun 13;276(5319):1719-24. doi: 10.1126/science.276.5319.1719.

Abstract

In allogeneic bone marrow transplantation (allo-BMT), donor lymphocytes play a central therapeutic role in both graft-versus-leukemia (GvL) and immune reconstitution. However, their use is limited by the risk of severe graft-versus-host disease (GvHD). Eight patients who relapsed or developed Epstein-Barr virus-induced lymphoma after T cell-depleted BMT were then treated with donor lymphocytes transduced with the herpes simplex virus thymidine kinase (HSV-TK) suicide gene. The transduced lymphocytes survived for up to 12 months, resulting in antitumor activity in five patients. Three patients developed GvHD, which could be effectively controlled by ganciclovir-induced elimination of the transduced cells. These data show that genetic manipulation of donor lymphocytes may increase the efficacy and safety of allo-BMT and expand its application to a larger number of patients.

Publication types

  • Clinical Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Bone Marrow Transplantation* / adverse effects
  • Ganciclovir / therapeutic use
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Graft vs Host Disease / etiology
  • Graft vs Host Disease / therapy*
  • Humans
  • Leukemia / immunology
  • Leukemia / therapy*
  • Lymphocyte Transfusion*
  • Lymphocytes / enzymology
  • Lymphoma, Non-Hodgkin / therapy
  • Lymphoproliferative Disorders / therapy
  • Pilot Projects
  • Simplexvirus / enzymology
  • Simplexvirus / genetics
  • Thymidine Kinase / genetics*
  • Transplantation, Homologous

Substances

  • Thymidine Kinase
  • Ganciclovir