Treatment of severe Evans syndrome with an allogeneic cord blood transplant

Bone Marrow Transplant. 1997 Sep;20(5):427-9. doi: 10.1038/sj.bmt.1700907.

Abstract

Immunosuppressive therapy is commonly used in the management of autoimmune disorders. As marrow-derived lymphocytes appear to play a key role in these diseases, lymphoid ablation followed by replacement with autologous or allogeneic stem cells may be a therapeutic option. We report a 5-year-old boy with severe Evans syndrome which consists of immune thrombocytopenia and Coombs-positive hemolytic anemia. He was rendered into complete remission with marrow ablation followed by rescue with an HLA-identical sibling cord blood transplant. He unexpectedly died 9 months following transplant from acute hepatic failure of unknown etiology.

MeSH terms

  • Anemia, Hemolytic, Autoimmune / therapy*
  • Autoimmune Diseases / therapy
  • Blood Transfusion
  • Child, Preschool
  • Fetal Blood / cytology*
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Male
  • Purpura, Thrombocytopenic, Idiopathic / therapy*
  • Syndrome
  • Transplantation, Homologous*