Treatment of iron overload in the "ex-thalassemic". Report from the phlebotomy program

Ann N Y Acad Sci. 1998 Jun 30:850:288-93. doi: 10.1111/j.1749-6632.1998.tb10485.x.

Abstract

After successful marrow transplantation (BMT) iron overload remains an important cause of morbidity in Thalassemia. After BMT, patients have normal erythropoiesis capable of producing a hyperplastic response to phlebotomy so that this procedure can be contemplated as a method of mobilizing iron from overloaded tissues. Forty-one patients (mean age 16 +/- 2.9 years) with prolonged follow-up (range 2-7 years) after BMT were submitted to a moderate intensity phlebotomy program (6 ml/kg blood withdrawal at 14-day intervals) to reduce iron overload. Values are expressed as mean +/- SD or as median with a range (25th-75th percentile). Serum ferritin decreased from 2,587 (2,129-4,817) to 280 (132-920) micrograms/l (p < 0.0001), total transferrin increased from 2.34 +/- 0.37 to 2.9 +/- 0.66 g/l (p = 0.0001), transferrin saturation decreased from 90% +/- 14% to 39% +/- 34% (p < 0.0001). Liver iron concentration evaluated on liver biopsy specimens decreased from 20.8 (15.5-28.1) to 3 (0.9-14.6) mg/g dry weight (p < 0.0001). Alanine amino-transaminase from 5.2 +/- 3.4 to 1.6 +/- 1.2 (p < 0.0001) times the upper level of normality. The histological grading for chronic hepatitis (Histology Activity Index) decreased from 4.2 +/- 2.4 to 2.3 +/- 1.8 (p < 0.0001). Phlebotomy is a safe, efficient, and widely applicable method to decrease iron overload in "ex-thalassemic."

Publication types

  • Multicenter Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Alanine Transaminase / blood
  • Bone Marrow Transplantation*
  • Female
  • Ferritins / blood
  • Follow-Up Studies
  • Humans
  • Iron / metabolism*
  • Liver / metabolism
  • Male
  • Morbidity
  • Phlebotomy*
  • Postoperative Complications / epidemiology
  • Postoperative Complications / therapy
  • Time Factors
  • Transferrin / metabolism
  • beta-Thalassemia / metabolism
  • beta-Thalassemia / therapy*

Substances

  • Transferrin
  • Ferritins
  • Iron
  • Alanine Transaminase