A human severe combined immunodeficiency (SCID) condition with increased sensitivity to ionizing radiations and impaired V(D)J rearrangements defines a new DNA recombination/repair deficiency

J Exp Med. 1998 Aug 17;188(4):627-34. doi: 10.1084/jem.188.4.627.

Abstract

The products of recombination activating gene (RAG)1 and RAG2 initiate the lymphoid-specific phase of the V(D)J recombination by creating a DNA double-strand break (dsb), leaving hairpin-sealed coding ends. The next step uses the general DNA repair machinery of the cells to resolve this dsb. Several genes involved in both V(D)J recombination and DNA repair have been identified through the analysis of in vitro mutants (Chinese hamster ovary cells) and in vivo situations of murine and equine severe combined immunodeficiency (scid). These studies lead to the description of the Ku-DNA-dependent protein kinase complex and the XRCC4 factor. A human SCID condition is characterized by an absence of B and T lymphocytes. One subset of these patients also demonstrates an increased sensitivity to the ionizing radiation of their fibroblasts and bone marrow precursor cells. This phenotype is accompanied by a profound defect in V(D)J recombination with a lack of coding joint formation, whereas signal joints are normal. Functional and genetic analyses distinguish these patients from the other recombination/repair mutants, and thus define a new group of mutants whose affected gene(s) is involved in sensitivity to ionizing radiation and V(D)J recombination.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antigens, Nuclear*
  • B-Lymphocytes / immunology*
  • Cell Line
  • Cell Line, Transformed
  • Cricetinae
  • Cricetulus
  • DNA Helicases*
  • DNA Repair* / radiation effects
  • DNA-Activated Protein Kinase
  • DNA-Binding Proteins / metabolism
  • Female
  • Gamma Rays
  • Gene Rearrangement* / radiation effects
  • Genes, Immunoglobulin*
  • Humans
  • Immunoglobulin Joining Region / genetics
  • Immunoglobulin Variable Region / genetics
  • Ku Autoantigen
  • Ligands
  • Male
  • Nuclear Proteins / metabolism
  • Pedigree
  • Protein Serine-Threonine Kinases / metabolism
  • Radiation Tolerance*
  • Severe Combined Immunodeficiency / genetics
  • Severe Combined Immunodeficiency / immunology*
  • T-Lymphocytes / immunology*

Substances

  • Antigens, Nuclear
  • DNA-Binding Proteins
  • Immunoglobulin Joining Region
  • Immunoglobulin Variable Region
  • Ligands
  • Nuclear Proteins
  • XRCC4 protein, human
  • DNA-Activated Protein Kinase
  • PRKDC protein, human
  • Protein Serine-Threonine Kinases
  • DNA Helicases
  • XRCC5 protein, human
  • Xrcc6 protein, human
  • Ku Autoantigen