Abstract
Two brothers with dystonia and slight MRI changes in the basal ganglia had normal urinary glutaric acid excretion, but slightly increased 3-hydroxyglutarate and conjugated glutarate excretions. Both siblings have high residual glutaryl-CoA dehydrogenase activity, and are compound heterozygotes for two mutations - R227P and V400M reported to be disease-causing in patients with glutaric aciduria type I.
Publication types
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Case Reports
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Research Support, Non-U.S. Gov't
MeSH terms
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Amino Acid Metabolism, Inborn Errors / genetics
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Amino Acid Metabolism, Inborn Errors / physiopathology*
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Child
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Glutarates / urine*
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Glutaryl-CoA Dehydrogenase
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Humans
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Male
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Nuclear Family
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Oxidoreductases / metabolism*
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Oxidoreductases Acting on CH-CH Group Donors*
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Point Mutation
Substances
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Glutarates
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Oxidoreductases
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Oxidoreductases Acting on CH-CH Group Donors
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Glutaryl-CoA Dehydrogenase