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Page 1
[Gene therapy: where do we stand?].
Cavazzana-Calvo M. Cavazzana-Calvo M. Rev Prat. 2013 Apr;63(4):457-61. Rev Prat. 2013. PMID: 23682464 French.
Gene therapy of primary T cell immunodeficiencies.
Fischer A, Hacein-Bey-Abina S, Cavazzana-Calvo M. Fischer A, et al. Among authors: cavazzana calvo m. Gene. 2013 Aug 10;525(2):170-3. doi: 10.1016/j.gene.2013.03.092. Epub 2013 Apr 10. Gene. 2013. PMID: 23583799 Free article. Review.
Outcomes of transplantation using various hematopoietic cell sources in children with Hurler syndrome after myeloablative conditioning.
Boelens JJ, Aldenhoven M, Purtill D, Ruggeri A, Defor T, Wynn R, Wraith E, Cavazzana-Calvo M, Rovelli A, Fischer A, Tolar J, Prasad VK, Escolar M, Gluckman E, O'Meara A, Orchard PJ, Veys P, Eapen M, Kurtzberg J, Rocha V; Eurocord; Inborn Errors Working Party of European Blood and Marrow Transplant group; Duke University Blood and Marrow Transplantation Program; Centre for International Blood and Marrow Research. Boelens JJ, et al. Among authors: cavazzana calvo m. Blood. 2013 May 9;121(19):3981-7. doi: 10.1182/blood-2012-09-455238. Epub 2013 Mar 14. Blood. 2013. PMID: 23493783 Free PMC article.
Characteristics and outcome of early-onset, severe forms of Wiskott-Aldrich syndrome.
Mahlaoui N, Pellier I, Mignot C, Jais JP, Bilhou-Nabéra C, Moshous D, Neven B, Picard C, de Saint-Basile G, Cavazzana-Calvo M, Blanche S, Fischer A. Mahlaoui N, et al. Among authors: cavazzana calvo m. Blood. 2013 Feb 28;121(9):1510-6. doi: 10.1182/blood-2012-08-448118. Epub 2012 Dec 20. Blood. 2013. PMID: 23264593 Free article.
Primary microcephaly, impaired DNA replication, and genomic instability caused by compound heterozygous ATR mutations.
Mokrani-Benhelli H, Gaillard L, Biasutto P, Le Guen T, Touzot F, Vasquez N, Komatsu J, Conseiller E, Pïcard C, Gluckman E, Francannet C, Fischer A, Durandy A, Soulier J, de Villartay JP, Cavazzana-Calvo M, Revy P. Mokrani-Benhelli H, et al. Among authors: cavazzana calvo m. Hum Mutat. 2013 Feb;34(2):374-84. doi: 10.1002/humu.22245. Epub 2012 Dec 20. Hum Mutat. 2013. PMID: 23111928
Gene therapy for primary immunodeficiencies: Part 1.
Cavazzana-Calvo M, Fischer A, Hacein-Bey-Abina S, Aiuti A. Cavazzana-Calvo M, et al. Curr Opin Immunol. 2012 Oct;24(5):580-4. doi: 10.1016/j.coi.2012.08.008. Epub 2012 Sep 12. Curr Opin Immunol. 2012. PMID: 22981681 Review.
Massive expansion of maternal T cells in response to EBV infection in a patient with SCID-Xl.
Touzot F, Dal-Cortivo L, Verkarre V, Lim A, Crucis-Armengaud A, Moshous D, Héritier S, Frange P, Kaltenbach S, Blanche S, Picard C, Hacein-Bey-Abina S, Cavazzana-Calvo M, Fischer A. Touzot F, et al. Among authors: cavazzana calvo m. Blood. 2012 Aug 30;120(9):1957-9. doi: 10.1182/blood-2012-04-426833. Blood. 2012. PMID: 22936741 Free article. No abstract available.
Gene therapy for primary immunodeficiencies: Part 2.
Aiuti A, Bacchetta R, Seger R, Villa A, Cavazzana-Calvo M. Aiuti A, et al. Among authors: cavazzana calvo m. Curr Opin Immunol. 2012 Oct;24(5):585-91. doi: 10.1016/j.coi.2012.07.012. Epub 2012 Aug 18. Curr Opin Immunol. 2012. PMID: 22909900 Review.
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency.
Hassan A, Booth C, Brightwell A, Allwood Z, Veys P, Rao K, Hönig M, Friedrich W, Gennery A, Slatter M, Bredius R, Finocchi A, Cancrini C, Aiuti A, Porta F, Lanfranchi A, Ridella M, Steward C, Filipovich A, Marsh R, Bordon V, Al-Muhsen S, Al-Mousa H, Alsum Z, Al-Dhekri H, Al Ghonaium A, Speckmann C, Fischer A, Mahlaoui N, Nichols KE, Grunebaum E, Al Zahrani D, Roifman CM, Boelens J, Davies EG, Cavazzana-Calvo M, Notarangelo L, Gaspar HB; Inborn Errors Working Party of the European Group for Blood and Marrow Transplantation and European Society for Immunodeficiency. Hassan A, et al. Among authors: cavazzana calvo m. Blood. 2012 Oct 25;120(17):3615-24; quiz 3626. doi: 10.1182/blood-2011-12-396879. Epub 2012 Jul 12. Blood. 2012. PMID: 22791287 Free article.
199 results