The role of the iminosugar N-butyldeoxynojirimycin (miglustat) in the management of type I (non-neuronopathic) Gaucher disease: a position statement.
Cox TM, Aerts JM, Andria G, Beck M, Belmatoug N, Bembi B, Chertkoff R, Vom Dahl S, Elstein D, Erikson A, Giralt M, Heitner R, Hollak C, Hrebicek M, Lewis S, Mehta A, Pastores GM, Rolfs A, Miranda MC, Zimran A; Advisory Council to the European Working Group on Gaucher Disease.
Cox TM, et al. Among authors: aerts jm.
J Inherit Metab Dis. 2003;26(6):513-26. doi: 10.1023/a:1025902113005.
J Inherit Metab Dis. 2003.
PMID: 14605497
Review.