Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy.
Romero NB, Braun S, Benveniste O, Leturcq F, Hogrel JY, Morris GE, Barois A, Eymard B, Payan C, Ortega V, Boch AL, Lejean L, Thioudellet C, Mourot B, Escot C, Choquel A, Recan D, Kaplan JC, Dickson G, Klatzmann D, Molinier-Frenckel V, Guillet JG, Squiban P, Herson S, Fardeau M.
Romero NB, et al. Among authors: guillet jg.
Hum Gene Ther. 2004 Nov;15(11):1065-76. doi: 10.1089/hum.2004.15.1065.
Hum Gene Ther. 2004.
PMID: 15610607
Clinical Trial.