Correction of a urea cycle defect after ex vivo gene editing of human hepatocytes.
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Mol Ther. 2021 May 5;29(5):1903-1917. doi: 10.1016/j.ymthe.2021.01.024. Epub 2021 Jan 21.
Mol Ther. 2021.
PMID: 33484963
Free PMC article.