Modelling pathogenesis and treatment of familial dysautonomia using patient-specific iPSCs.
Lee G, Papapetrou EP, Kim H, Chambers SM, Tomishima MJ, Fasano CA, Ganat YM, Menon J, Shimizu F, Viale A, Tabar V, Sadelain M, Studer L.
Lee G, et al. Among authors: chambers sm.
Nature. 2009 Sep 17;461(7262):402-6. doi: 10.1038/nature08320. Epub 2009 Aug 19.
Nature. 2009.
PMID: 19693009
Free PMC article.