Gorbatyuk M - Search Results

1

In vivo RNAi-mediated alpha-synuclein silencing induces nigrostriatal degeneration.

Gorbatyuk OS, Li S, Nash K, Gorbatyuk M, Lewin AS, Sullivan LF, Mandel RJ, Chen W, Meyers C, Manfredsson FP, Muzyczka N. Gorbatyuk OS, et al. Among authors: gorbatyuk m. Mol Ther. 2010 Aug;18(8):1450-7. doi: 10.1038/mt.2010.115. Epub 2010 Jun 15. Mol Ther. 2010. PMID: 20551914 Free PMC article.

2

Design and validation of therapeutic hammerhead ribozymes for autosomal dominant diseases.

Fritz JJ, Gorbatyuk M, Lewin AS, Hauswirth WW. Fritz JJ, et al. Among authors: gorbatyuk m. Methods Mol Biol. 2004;252:221-36. doi: 10.1385/1-59259-746-7:221. Methods Mol Biol. 2004. PMID: 15017052

3

Knockdown of wild-type mouse rhodopsin using an AAV vectored ribozyme as part of an RNA replacement approach.

Gorbatyuk MS, Pang JJ, Thomas J Jr, Hauswirth WW, Lewin AS. Gorbatyuk MS, et al. Mol Vis. 2005 Aug 29;11:648-56. Mol Vis. 2005. PMID: 16145542 Free article.

4

Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.

Gorbatyuk M, Justilien V, Liu J, Hauswirth WW, Lewin AS. Gorbatyuk M, et al. Exp Eye Res. 2007 Jan;84(1):44-52. doi: 10.1016/j.exer.2006.08.014. Epub 2006 Nov 1. Exp Eye Res. 2007. PMID: 17083931 Free PMC article.

5

Suppression of mouse rhodopsin expression in vivo by AAV mediated siRNA delivery.

Gorbatyuk M, Justilien V, Liu J, Hauswirth WW, Lewin AS. Gorbatyuk M, et al. Vision Res. 2007 Apr;47(9):1202-8. doi: 10.1016/j.visres.2006.11.026. Epub 2007 Feb 12. Vision Res. 2007. PMID: 17292939 Free PMC article.

6

Down-regulation of expression of rat pyruvate dehydrogenase E1alpha gene by self-complementary adeno-associated virus-mediated small interfering RNA delivery.

Han Z, Gorbatyuk M, Thomas J Jr, Lewin AS, Srivastava A, Stacpoole PW. Han Z, et al. Among authors: gorbatyuk m. Mitochondrion. 2007 Jul;7(4):253-9. doi: 10.1016/j.mito.2007.02.003. Epub 2007 Feb 20. Mitochondrion. 2007. PMID: 17392036 Free PMC article.

7

Gene therapy for mouse models of ADRP.

Gorbatyuk MS, Hauswirth WW, Lewin AS. Gorbatyuk MS, et al. Adv Exp Med Biol. 2008;613:107-12. doi: 10.1007/978-0-387-74904-4_11. Adv Exp Med Biol. 2008. PMID: 18188934 No abstract available.

8

Restoration of visual function in P23H rhodopsin transgenic rats by gene delivery of BiP/Grp78.

Gorbatyuk MS, Knox T, LaVail MM, Gorbatyuk OS, Noorwez SM, Hauswirth WW, Lin JH, Muzyczka N, Lewin AS. Gorbatyuk MS, et al. Among authors: gorbatyuk os. Proc Natl Acad Sci U S A. 2010 Mar 30;107(13):5961-6. doi: 10.1073/pnas.0911991107. Epub 2010 Mar 15. Proc Natl Acad Sci U S A. 2010. PMID: 20231467 Free PMC article.

9

AAV delivery of wild-type rhodopsin preserves retinal function in a mouse model of autosomal dominant retinitis pigmentosa.

Mao H, James T Jr, Schwein A, Shabashvili AE, Hauswirth WW, Gorbatyuk MS, Lewin AS. Mao H, et al. Hum Gene Ther. 2011 May;22(5):567-75. doi: 10.1089/hum.2010.140. Epub 2011 Mar 7. Hum Gene Ther. 2011. PMID: 21126223 Free PMC article.

10

Functional rescue of P23H rhodopsin photoreceptors by gene delivery.

Gorbatyuk MS, Gorbatyuk OS, LaVail MM, Lin JH, Hauswirth WW, Lewin AS. Gorbatyuk MS, et al. Among authors: gorbatyuk os. Adv Exp Med Biol. 2012;723:191-7. doi: 10.1007/978-1-4614-0631-0_26. Adv Exp Med Biol. 2012. PMID: 22183333 Free PMC article.

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