PABPN1 gene therapy for oculopharyngeal muscular dystrophy.
Malerba A, Klein P, Bachtarzi H, Jarmin SA, Cordova G, Ferry A, Strings V, Espinoza MP, Mamchaoui K, Blumen SC, St Guily JL, Mouly V, Graham M, Butler-Browne G, Suhy DA, Trollet C, Dickson G.
Malerba A, et al. Among authors: ferry a.
Nat Commun. 2017 Mar 31;8:14848. doi: 10.1038/ncomms14848.
Nat Commun. 2017.
PMID: 28361972
Free PMC article.