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Dual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis.
Chiriaco M, Farinelli G, Capo V, Zonari E, Scaramuzza S, Di Matteo G, Sergi LS, Migliavacca M, Hernandez RJ, Bombelli F, Giorda E, Kajaste-Rudnitski A, Trono D, Grez M, Rossi P, Finocchi A, Naldini L, Gentner B, Aiuti A. Chiriaco M, et al. Among authors: capo v. Mol Ther. 2014 Aug;22(8):1472-1483. doi: 10.1038/mt.2014.87. Epub 2014 May 29. Mol Ther. 2014. PMID: 24869932 Free PMC article.
Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis.
Capo V, Penna S, Merelli I, Barcella M, Scala S, Basso-Ricci L, Draghici E, Palagano E, Zonari E, Desantis G, Uva P, Cusano R, Sergi Sergi L, Crisafulli L, Moshous D, Stepensky P, Drabko K, Kaya Z, Unal E, Gezdirici A, Menna G, Serafini M, Aiuti A, Locatelli SL, Carlo-Stella C, Schulz AS, Ficara F, Sobacchi C, Gentner B, Villa A. Capo V, et al. Haematologica. 2021 Jan 1;106(1):74-86. doi: 10.3324/haematol.2019.238261. Haematologica. 2021. PMID: 31949009 Free PMC article.
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Schiroli G, Ferrari S, Conway A, Jacob A, Capo V, Albano L, Plati T, Castiello MC, Sanvito F, Gennery AR, Bovolenta C, Palchaudhuri R, Scadden DT, Holmes MC, Villa A, Sitia G, Lombardo A, Genovese P, Naldini L. Schiroli G, et al. Among authors: capo v. Sci Transl Med. 2017 Oct 11;9(411):eaan0820. doi: 10.1126/scitranslmed.aan0820. Sci Transl Med. 2017. PMID: 29021165
Murine Rankl-/- Mesenchymal Stromal Cells Display an Osteogenic Differentiation Defect Improved by a RANKL-Expressing Lentiviral Vector.
Schena F, Menale C, Caci E, Diomede L, Palagano E, Recordati C, Sandri M, Tampieri A, Bortolomai I, Capo V, Pastorino C, Bertoni A, Gattorno M, Martini A, Villa A, Traggiai E, Sobacchi C. Schena F, et al. Among authors: capo v. Stem Cells. 2017 May;35(5):1365-1377. doi: 10.1002/stem.2574. Epub 2017 Mar 1. Stem Cells. 2017. PMID: 28100034
Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation.
Capo V, Castiello MC, Fontana E, Penna S, Bosticardo M, Draghici E, Poliani LP, Sergi Sergi L, Rigoni R, Cassani B, Zanussi M, Carrera P, Uva P, Dobbs K, Sacchetti N, Notarangelo LD, van Til NP, Wagemaker G, Villa A. Capo V, et al. J Allergy Clin Immunol. 2018 Sep;142(3):928-941.e8. doi: 10.1016/j.jaci.2017.11.015. Epub 2017 Dec 11. J Allergy Clin Immunol. 2018. PMID: 29241731 Free PMC article.
One Disease, Many Genes: Implications for the Treatment of Osteopetroses.
Penna S, Capo V, Palagano E, Sobacchi C, Villa A. Penna S, et al. Among authors: capo v. Front Endocrinol (Lausanne). 2019 Feb 19;10:85. doi: 10.3389/fendo.2019.00085. eCollection 2019. Front Endocrinol (Lausanne). 2019. PMID: 30837952 Free PMC article. Review.
Autosomal recessive osteopetrosis: mechanisms and treatments.
Penna S, Villa A, Capo V. Penna S, et al. Among authors: capo v. Dis Model Mech. 2021 May 1;14(5):dmm048940. doi: 10.1242/dmm.048940. Epub 2021 May 10. Dis Model Mech. 2021. PMID: 33970241 Free PMC article. Review.
82 results