In vivo CRISPR-Cas9 genome editing in mice identifies genetic modifiers of somatic CAG repeat instability in Huntington's disease.
Mouro Pinto R, Murtha R, Azevedo A, Douglas C, Kovalenko M, Ulloa J, Crescenti S, Burch Z, Oliver E, Kesavan M, Shibata S, Vitalo A, Mota-Silva E, Riggs MJ, Correia K, Elezi E, Demelo B, Carroll JB, Gillis T, Gusella JF, MacDonald ME, Wheeler VC.
Mouro Pinto R, et al. Among authors: macdonald me.
Nat Genet. 2025 Jan 22. doi: 10.1038/s41588-024-02054-5. Online ahead of print.
Nat Genet. 2025.
PMID: 39843658