Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease.
Uchida N, Drysdale CM, Nassehi T, Gamer J, Yapundich M, DiNicola J, Shibata Y, Hinds M, Gudmundsdottir B, Haro-Mora JJ, Demirci S, Tisdale JF.
Uchida N, et al.
Mol Ther Methods Clin Dev. 2021 Mar 3;21:121-132. doi: 10.1016/j.omtm.2021.02.022. eCollection 2021 Jun 11.
Mol Ther Methods Clin Dev. 2021.
PMID: 33816645
Free PMC article.