Effect of the Histone Deacetylase Inhibitor FRM-0334 on Progranulin Levels in Patients With Progranulin Gene Haploinsufficiency: A Randomized Clinical Trial.
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Ljubenkov PA, et al. Among authors: goodman ij.
JAMA Netw Open. 2021 Sep 1;4(9):e2125584. doi: 10.1001/jamanetworkopen.2021.25584.
JAMA Netw Open. 2021.
PMID: 34559230
Free PMC article.
Clinical Trial.