Liver-directed gene therapy corrects cardiovascular lesions in feline mucopolysaccharidosis type I.
Hinderer C, Bell P, Gurda BL, Wang Q, Louboutin JP, Zhu Y, Bagel J, O'Donnell P, Sikora T, Ruane T, Wang P, Haskins ME, Wilson JM.
Hinderer C, et al. Among authors: bell p.
Proc Natl Acad Sci U S A. 2014 Oct 14;111(41):14894-9. doi: 10.1073/pnas.1413645111. Epub 2014 Sep 29.
Proc Natl Acad Sci U S A. 2014.
PMID: 25267637
Free PMC article.