Online self-report data for duchenne muscular dystrophy confirms natural history and can be used to assess for therapeutic benefits.
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PLoS Curr. 2014 Oct 17;6:ecurrents.md.e1e8f2be7c949f9ffe81ec6fca1cce6a. doi: 10.1371/currents.md.e1e8f2be7c949f9ffe81ec6fca1cce6a.
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PMID: 25635234
Free PMC article.