Dominant variants in the splicing factor PUF60 cause a recognizable syndrome with intellectual disability, heart defects and short stature.
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El Chehadeh S, et al.
Eur J Hum Genet. 2016 Jan;25(1):43-51. doi: 10.1038/ejhg.2016.133. Epub 2016 Nov 2.
Eur J Hum Genet. 2016.
PMID: 27804958
Free PMC article.